幹細胞治療醫學報告
以淺顯語言整理已發表的幹細胞治療研究,依疾病分類。每份摘要都連結到經同行評審的原始研究。
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The Journal of Pediatrics · 2020-05-19
靜脈輸注臍帶血治療自閉症譜系障礙兒童的2期隨機臨床試驗:研究摘要
Geraldine Dawson, Jessica M. Sun, Jennifer Baker, Kimberly Carpenter, Scott Compton, Megan Deaver, Lauren Franz, Nicole Heilbron, Brianna Herold, Joseph Horrigan, Jill Howard, Andrzej Kosinski, Samantha Major, Michael Murias, Kristin Page, Vinod K. Prasad, Maura Sabatos-DeVito, Fred Sanfilippo, Linmarie Sikich, Ryan Simmons, Allen Song, Saritha Vermeer, Barbara Waters-Pick, Jesse Troy, and Joanne Kurtzberg.
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Stem Cells Translational Medicine · 2020-06-12
自閉症譜系障礙兒童輸注人類臍帶組織間質基質細胞:研究摘要
Jessica M. Sun, Geraldine Dawson, Lauren Franz, Jill Howard, Colleen McLaughlin, Bethany Kistler, Barbara Waters-Pick, Norin Meadows, Jesse Troy, and Joanne Kurtzberg.
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Stem Cell Research & Therapy · 2023-04-27
具免疫調節作用的羊膜來源間質基質細胞在裘馨氏肌營養不良症小鼠模型中保存肌肉功能
Yuko Nitahara-Kasahara, Soya Nakayama, Koichi Kimura, Sho Yamaguchi, Yuko Kakiuchi, Chikako Nito, Masahiro Hayashi, Tomoyuki Nakaishi, Yasuyoshi Ueda, and Takashi Okada.
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Stem Cells Translational Medicine · 2021-07-27
臍帶來源間質幹細胞用於肌營養不良症患者:來自真實世界同情使用的結果
Beata Świątkowska-Flis, Izabela Zdolińska-Malinowska, Dominika Sługocka, and Dariusz Boruczkowski.
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Neural Regeneration Research · 2025-06-19
外傷性視神經病變的細胞療法:最新進展、挑戰與展望
Yuanhui Wang, Moxin Chen, Zhimin Tang and Ping Gu.
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Cellular and Molecular Life Sciences · 2025-10-11
裘馨氏肌營養不良症的細胞療法:前景、挑戰與爭議
Agnieszka Łoboda and Józef Dulak.
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The Lancet · 2026-07-29
Deramiocel心臟來源細胞療法用於晚期裘馨氏肌營養不良症(HOPE-3):一項3期隨機、雙盲、安慰劑對照試驗
Craig M McDonald, Chet Villa, Jonathan H Soslow, Kati Maharry, Nathaniel Hogan, Michael Binks, Kevin C Berth, Kristi A Elliott, Michael Taylor, Kan N Hor, James Signorovich, Erik K Henricson, Han C Phan, Susan Apkon, Partha S Ghosh, Cuixia Tian, Aravindhan Veerapandiyan, Leigh Ramos-Platt, Katheryn Gambetta, Saunder M Bernes, Arun S Varadhachary, Susan T Iannaccone, Chamindra G Laverty, Seth J Perlman, Nancy E Bass, Kathryn Mosher, Russell J Butterfield, Katherine D Mathews, Rebecca J Scharf, Edward C Smith, Jane Anne Emerson, Eugenio Mercuri, Mark S Awadalla, Linda Marbán, and Eduardo Marbán, on behalf of the HOPE-3 Investigators.
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Stem Cell Research & Therapy · 2026-06-19
異體臍帶血單核細胞用於伴有免疫失調之自閉症兒童的療效與安全性:研究摘要
Ziyan Zhang, Guanglei Wang, Fang Han, Honghui Zhou, Yan Liang, Li Zhang, Ping Pang, Xinyu Cao, Peili Hu, Xinyun Yao, Chunhua Sun, Jing Wang, Xiuyu Shi, Linyan Hu, and Guang Yang.
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BMC Ophthalmology · 2024-07-29
評估間質幹細胞治療對視神經病變患者視力與視網膜神經纖維層厚度的影響:一項全面的系統性回顧與統合分析
Samira Chaibakhsh, Fatemeh Azimi, Alireza Shoae-Hassani, Parvin Niknam, Ali Ghamari, Samaneh Dehghan and Naveed Nilforushan.
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Stem Cell Research & Therapy · 2023-09-21
玻璃體內同種異體間質幹細胞:一項針對急性非動脈炎性視神經病變的非隨機2期臨床試驗
Jose C. Pastor, Salvador Pastor-Idoate, Marina López-Paniagua, Marta Para, Francisco Blazquez, Esther Murgui, Verónica García and Rosa M. Coco-Martín.
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Stem Cell Reviews and Reports · 2025-12-18
全身性DT-DEC01細胞療法用於無法行走的裘馨氏肌營養不良症患者的長期安全性與療效:一項為期24個月的臨床評估
Maria Siemionow, Grzegorz Biegański, Adam Niezgoda, Agnieszka Sobkowiak-Sobierajska, Jarosław Czarnota, Krzysztof Siemionow, Anna Ziemiecka, Katarzyna Bożyk, and Jacek Wachowiak.
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Journal of Translational Medicine · 2026-03-20
以間質幹細胞/基質細胞為基礎的自閉症譜系障礙治療:新證據與臨床前景:研究摘要
Minghui Xu, Xiaohan Zhang, Yuqian Liu, Yue Yang, Zijing Zhou, Jun Ma, and Sanbing Shen.
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The Lancet · 2022-03-12
晚期裘馨氏肌營養不良症的重複靜脈注射心球來源細胞治療(HOPE-2):一項多中心、隨機、雙盲、安慰劑對照的第2期試驗
Craig M McDonald, Eduardo Marbán, Suzanne Hendrix, Nathaniel Hogan, Rachel Ruckdeschel Smith, Michelle Eagle, Richard S Finkel, Cuixia Tian, Joanne Janas, Matthew M Harmelink, Arun S Varadhachary, Michael D Taylor, Kan N Hor, Oscar H Mayer, Erik K Henricson, Pat Furlong, Deborah D Ascheim, Siegfried Rogy, Paula Williams, Linda Marbán, and the HOPE-2 Study Group.
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Molecular Neurodegeneration · 2023-09-21
視神經病變中視網膜神經節細胞再填充以恢復視力:RReSTORe聯盟的路線圖
Jonathan R. Soucy, Erika A. Aguzzi, Julie Cho, Michael James Gilhooley, Casey Keuthan, Ziming Luo, Aboozar Monavarfeshani, Meher A. Saleem, Xue-Wei Wang, Juilette Wohlschlegel, The RReSTORe Consortium, Petr Baranov, Adriana Di Polo, Brad Fortune, Kimberly K. Gokoffski, Jeffrey L. Goldberg, William Guido, Alex L. Kolodkin, Carol A. Mason, Yvonne Ou, Thomas A. Reh, Ahmara G. Ross, Brian C. Samuels, Derek Welsbie, Donald J. Zack and Thomas V. Johnson.
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Journal of Clinical Neurology · 2025-01-01
華通氏膠來源間質幹細胞用於裘馨氏肌營養不良症患者的安全性與耐受性:一項第1期臨床研究
Jiwon Lee, Sang Eon Park, Mira Kim, Hyeongseop Kim, Jeong-Yi Kwon, Hong Bae Jeon, Jong Wook Chang, and Jeehun Lee.
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European Psychiatry (European Psychiatric Association congress abstract, Vol. 69 Suppl. 1, p. S534) · 2026-07-31
幹細胞治療自閉症譜系障礙:臨床證據的系統性回顧與統合分析(會議摘要):研究摘要
S. M. M. Fekrat, V. Sharma, S. Prasad, and S. Gunturu.
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Frontiers in Cell and Developmental Biology · 2026-03-04
骨髓間質幹細胞來源外泌體對視網膜和視神經疾病的治療潛力
Mingzhe Shi, Shounan Qi, Feifan Qi and Chenguang Wang.
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Stem Cell Research & Therapy · 2026-07-30
自閉症譜系障礙三次重複鞘內注射異體臍帶來源間質基質細胞:1期臨床試驗:研究摘要
Elaheh Khodadoust, Hadi Zarafshan, Masoumeh Nouri, Anahita Majmaa, Ali Khaleghi, Fatemeh Zamani, Milad Seyfi, Mohammad Amin Shahrbaf, Solaleh Samimi, Bahareh Sadri, Seyedeh Malihe Mahmoodi, Norouz Abdi, Ali Ghasemi, Mahmoud Reza Ashrafi, Morteza Zarrabi, Massoud Vosough, and Mohammad Reza Mohammadi.
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Stem Cell Investigation · 2019-12-05
幹細胞眼科治療研究(SCOTS):骨髓來源幹細胞治療顯性視神經萎縮
Jeffrey N. Weiss, Steven Levy.
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